Design Therapeutics, Inc. is a biopharmaceutical company specializing in the development of drugs for genetic diseases and neurodegenerative disorders. Their main focus is on discovering and developing therapeutics aimed at correcting defective genetic mechanisms associated with these diseases. The company utilizes modern technologies such as RNA therapy, CRISPR-Cas9, and small molecule chemistry to identify and develop new drug molecules with the potential to modify the course of genetically inherited diseases. Design Therapeutics, Inc. aims to bring innovative therapeutic approaches to patients suffering from genetic and neurodegenerative diseases in order to improve their quality of life.